A new hope for patients suffering from potentially fatal rare heart disease: NUHCS is first in Asia to recruit patients for landmark gene editing clinical trial
May 14, 2025
Singapore, May 14: While receiving treatment for a car accident ten years ago, Mr Chua learnt that he had an abnormal build-up of protein in his heart vessels. This discovery led to the diagnosis of a condition known as transthyretin amyloid cardiomyopathy (ATTR-CM), a rare disease currently affecting approximately 150 patients in Singapore. The international study explores gene editing therapy to stop the production of proteins causing the disease in ATTR-CM patients.
Read More ..
